Novel inhalable gene therapy trialed for people with cystic fibrosis
An inhalable medicine with the potential to improve lung disease in people with cystic fibrosis, irrespective of their ...
Hosted on MSN4d
Narberth Nonprofit Stress Relief Outlet for People with Cystic Fibrosis
Take A Breather Foundation, a Narberth-based nonprofit, provides much-needed stress relief outlet for individuals living with ...
Medscape11d
Novel Triple Combination Therapy May Transform Cystic Fibrosis Care in Children
Once-daily vanzacaftor-tezacaftor-deutivacaftor was safe and well-tolerated in children with cystic fibrosis, while ...
IFLScience on MSN8d
Inhalable Cystic Fibrosis Gene Therapy 24 Years In The Making Enters Clinical Trials
A new inhalable gene therapy for cystic fibrosis (CF) has entered Phase I clinical trials, a major milestone on the journey ...
Parents express concerns over effort to end NH Vaccine Association at State House
Parents are expressing concerns over an effort at the State House to eliminate the New Hampshire Vaccine Association, with some asking lawmakers to consider the plight of children who face significant ...
Business Insider9d
Boehringer Ingelheim and partners start clinical development of a first-in-class, inhaled gene therapy for people with cystic fibrosis
Ingelheim, Germany, 20 February 2025 – Boehringer Ingelheim, IP Group, the UK Respiratory Gene Therapy Consortium (GTC) 1 and OXB, 1 today announce the start of LENTICLAIR TM 1, a Phase I/II trial of ...
Vertex Pharmaceuticals gets CHMP opinion recommending Kaftrio label expansion
Vertex Pharmaceuticals (VRTX) announced that the European Medicines Agency’s Committee for Medicinal Products for Human Use adopted an opinion ...
Parents of at-risk children urge lawmakers to reject repeal of NH Vaccine Association
Some parents are worried about legislation moving forward at the State House that would dissolve the New Hampshire Vaccine ...
Medindia6d
Inhalable Gene Therapy Trialed for Cystic Fibrosis Patients
Researchers trial inhalable gene therapy for cystic fibrosis, offering a potential breakthrough in treating the genetic lung ...
EurekAlert!10d
Novel inhalable gene therapy trialled for people with cystic fibrosis
An inhalable medicine with the potential to improve lung disease in people with cystic fibrosis, irrespective of their mutation type, is being tested in human trials in the UK and Europe.